Explore how antisense oligonucleotides (ASOs) are transforming medicine by precisely controlling gene expression without altering DNA, offering new hope for genetic disorders.
Breakthroughs in combined growth factor and gene therapy for cochlear hair cell regeneration and hearing recovery.
Exploring how CRISPR gene editing is being used to reactivate fetal hemoglobin as a potential cure for sickle cell disease and beta-thalassemia.